LONGEFI
Company · Public · NTLA

Intellia Therapeutics

Clinical-stage genome editing company with in vivo CRISPR programmes in amyloidosis and hereditary angioedema.

EvidenceStrongDurability extended
Listing
Public
Ticker
NTLA
Headquarters
Cambridge, US
Founded
2014
Technology
In vivo CRISPR gene editing
Category
Market cap
$2.4B

Longevity thesis

Durable in vivo editing turns chronic disease management into single-administration treatment — the delivery template later longevity interventions will need.

Pipeline

ProgrammeStageFocus
NTLA-2002Phase 3Hereditary angioedema
nex-zPhase 3ATTR amyloidosis

Recent developments

  • 5 Aug 2026Reported extended durability of knockdown at 24 months.

Scientific evidence

EvidenceStrong

Human Phase 3 data with multi-year durability follow-up.

LONGEFI analysis

Relevant to longevity mainly as delivery-platform validation. Each durability update makes in vivo editing of aging-related targets more plausible.

Analysis is research commentary. It is not investment advice or a recommendation.