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Company · Public · BEAM

Beam Therapeutics

Precision genetic medicine company using base editing to make single-letter DNA changes without double-strand breaks.

EvidenceModerateProgramme on track
Listing
Public
Ticker
BEAM
Headquarters
Cambridge, US
Founded
2017
Technology
Base editing
Category
Market cap
$2.1B

Longevity thesis

Lower-risk editing chemistry broadens the set of diseases — and eventually risk genes — that can be safely addressed.

Pipeline

ProgrammeStageFocus
BEAM-101Phase 1/2Sickle cell disease
BEAM-302Phase 1/2Alpha-1 antitrypsin deficiency

Recent developments

  • 30 Jun 2026Reported corrected protein levels in AATD patients.

Scientific evidence

EvidenceModerate

Early human efficacy in monogenic disease.

LONGEFI analysis

A technical bellwether: base editing safety data shape how regulators may later view preventive genetic intervention.

Analysis is research commentary. It is not investment advice or a recommendation.